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Tag: Duchenne
2 items with this tag.
Mar 18, 2026
Duan_2018_micro_dystrophin_AAV
AAV
dual-vector
mini-gene
Duchenne
micro-dystrophin
gene-therapy
large-gene-delivery
Mar 18, 2026
Mendell_2020_micro_dystrophin_clinical
AAV
clinical-trial
micro-dystrophin
Duchenne
Phase1-2
rAAVrh74
gene-therapy
pediatric