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Tag: AAV
3 items with this tag.
Mar 18, 2026
Gadenstaetter_2024_inner_ear_gene_therapy_review
gene-therapy
inner-ear
cochlea
review
AAV
clinical-translation
bench-to-bedside
Mar 18, 2026
Mendell_2020_micro_dystrophin_clinical
AAV
clinical-trial
micro-dystrophin
Duchenne
Phase1-2
rAAVrh74
gene-therapy
pediatric
Mar 18, 2026
Omichi_2020_AAV_hair_cell_transduction
AAV
cochlea
hair-cell
transduction
serotype
gene-therapy
OHC
IHC